IMPROVING PATIENT EXPERIENCE WITHIN CLINICAL TRIALS & LONG TERM FOLLOW UP
13:30 – CHAIR INTRODUCTION
Chair: Dr Stephan Grupp, Medical Director Cell & Gene Therapy Lab, Children’s Hospital of Philadelphia
13:35 – CASE STUDY: IMPROVING PATIENT EXPERIENCE THROUGH THE DRUG DEVELOPMENT PATHWAY USING TREAT-NMD NETWORK
Speaker: David Allison, Chief Executive, Treat NMD Neuromuscular Network
13:50 – CASE STUDY: USE OF CTL019 IN PEDIATRIC ALL: A 17 YEAR OLD WITH REFRACTORY ALL COMPLETES 10 YEARS OF CAR-T FOLLOW UP
Speaker: Dr Stephan Grupp, Medical Director Cell & Gene Therapy Lab, Children’s Hospital of Philadelphia
14:05 – CASE STUDY:
Speaker:
14:20 – PANEL DISCUSSION
Speakers: