IMPROVING PATIENT EXPERIENCE WITHIN CLINICAL TRIALS & LONG TERM FOLLOW UP

31 Aug 2022
13:30

13:30 – CHAIR INTRODUCTION

Chair: Dr Stephan Grupp, Medical Director Cell & Gene Therapy Lab, Children’s Hospital of Philadelphia 

 

13:35 – CASE STUDY: IMPROVING PATIENT EXPERIENCE THROUGH THE DRUG DEVELOPMENT PATHWAY USING TREAT-NMD NETWORK 

Speaker: David Allison, Chief Executive, Treat NMD Neuromuscular Network

 

13:50 – CASE STUDY: USE OF CTL019 IN PEDIATRIC ALL: A 17 YEAR OLD WITH REFRACTORY ALL COMPLETES 10 YEARS OF CAR-T FOLLOW UP

Speaker: Dr Stephan Grupp, Medical Director Cell & Gene Therapy Lab, Children’s Hospital of Philadelphia

 

14:05 – CASE STUDY:

Speaker: 

 

14:20 – PANEL DISCUSSION

Speakers: 

David Allison, Chief Executive, Treat NMD Neuromuscular Network

Speakers

Stephan Grupp
Medical Director Cell & Gene Therapy Lab
Children’s Hospital of Philadelphia
David Allison
Chief Executive
TREAT-NMD
Melanie Calvert
Professor of Outcomes Methodology
University of Birmingham CPROR
Lee Aiyegbusi
Deputy Director Centre for Patient-Reported Outcomes Research (CPROR)
University of Birmingham CPROR